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Hematological Diseases

What are the most common hematological diseases in children?

The most frequent conditions in pediatric hematology include:

Red Blood Cell Disorders

  • Anemias due to membrane defects: hereditary spherocytosis
     
  • Enzyme deficiency anemias: glucose-6-phosphate dehydrogenase (G6PD) deficiency, pyruvate kinase (PK) deficiency
     
  • Hemoglobin disorders: sickle cell disease, methemoglobinemia, thalassemia, other hemoglobinopathies
     
  • Immune hemolytic anemias: transfusion-related, hemolytic disease of the newborn, cold antibody hemolytic anemia, warm antibody hemolytic anemia, paroxysmal cold hemoglobinuria, drug-induced hemolytic anemia
     
  • Hypersplenism
     
  • Aregenerative anemias: Diamond-Blackfan anemia, transient erythroblastopenia, bone marrow aplasia, congenital dyserythropoiesis, myelodysplastic syndromes
     
  • Iron deficiency anemia, anemia of chronic disease, megaloblastic anemia

Bone Marrow Failure Syndromes

  • Acquired aplastic anemia, Fanconi anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH), erythroblastopenia, amegakaryocytic thrombocytopenia

Myeloid Disorders

  • Neutropenia, neutrophilia, myelodysplastic syndromes, myeloproliferative disorders

Lymphoid Disorders

  • Lymphocytosis, lymphopenia, lymphadenopathy, splenomegaly, hypersplenism

Platelet Disorders

  • Central thrombocytopenias, immune thrombocytopenia (ITP), essential thrombocythemia, secondary thrombocytosis

Coagulation Disorders

  • Bleeding disorders, congenital and acquired coagulation disorders (hemophilia, von Willebrand disease), thrombophilia

Other Hematologic Disorders

  • Congenital or acquired immunodeficiencies, storage diseases